Lysosomal Storage Disorders: Optimizing the Transition From Child to Adult Care

Educational Objectives

What Is Nephropathic Cystinosis?

Clinical Manifestations of Nephropathic Cystinosis

Transition vs Transfer

Critical Components of the Transition Process

Critical Components of the Transition Process (cont)

Critical Components of the Transition Process (cont)

Few Clinicians Are Trained to Care for Children and Adults With Cystinosis

Cysteamine Therapy

Cysteamine Therapy (cont)

Patterns of Posttransplant Adherence

Risk Factors for Posttransplant Nonadherence

Strategies for Dealing with Nonadherence

Conclusions

References

References (cont)

References (cont)