New Horizons in Cystic Fibrosis Clinical Developments From Fall 2014

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Presentation transcript:

New Horizons in Cystic Fibrosis Clinical Developments From Fall 2014

New Data on Mutation-Targeting Therapies and Antibiotics

Combining Lumicaftor and Ivacaftor: The Results of TRAFFIC and TRANSPORTa,b

Methods

Results

Results (cont)

Summary

Study of an Investigational S-Nitroglutathione Reductase Inhibitor

Methods

Results

Results (cont)

Doxycycline Adjunctive Therapy

Methods

Clinical Results

Bioactivity Results

Conclusions

Reports on Investigational Mucolytic Agents and CFTR-Directed Therapies

Study of a Novel Mucolytic Agent

Assessing Viscosity

Assessing Transportability

Investigational CFTR Corrector Added to Ivacaftor Treatment

Methods

Methods and Results

Mean Within-Group Changes (Days 0 to 28)

Take-Home Points

Recent Reports on Pseudomonas Incidence and Treatment

Respiratory Microbiologic Trends

Methods and Results

Results

Results (cont)

Long-Term Data From EPIC Study

Results

Conclusions

Predictors of Response to Antibiotic Treatment for Pulmonary Exacerbations

Results (cont)

Conclusions

Introducing the STOP Study on Pulmonary Exacerbations

The STOP Study

Methods

Results

Physician Willingness to Enroll Patients in Interventional Trials

Preexacerbation Clinical Characteristics: STOP

Symptoms and Signs Present on Admission

Inhaled Hypertonic Saline Plus rhDNase

Results

Abbreviations

Abbreviations (cont)

References

References (cont)

References (cont)

References (cont)

References (cont)