733. Somatically Repairing Compound Heterozygous Recessive Mutations by Chromosomal Cut-and-Paste for In Vivo Gene Therapy  Dan Wang, Haiwei Mou, Karen.

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733. Somatically Repairing Compound Heterozygous Recessive Mutations by Chromosomal Cut-and-Paste for In Vivo Gene Therapy  Dan Wang, Haiwei Mou, Karen Tran, Jia Li, Blake Y. Wang, Dominic J. Gessler, Phillip WL Tai, Qin Su, Wen Xue, Guangping Gao  Molecular Therapy  Volume 24, (May 2016) DOI: 10.1016/S1525-0016(16)33541-9 Copyright © 2016 The American Society of Gene & Cell Therapy Terms and Conditions

Molecular Therapy 2016 24, DOI: (10.1016/S1525-0016(16)33541-9) Copyright © 2016 The American Society of Gene & Cell Therapy Terms and Conditions

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