Optimizing Joint Health in Hemophilia
This program will include a discussion of investigational agents not approved by the FDA for use in the United States.
Introduction
Prophylaxis Studies and Joint Health
Challenges to Prophylaxis
Introducing Prophylaxis
Inhibitors
Discussing Prophylaxis Risk With Patients
Overview of EHL Factor Concentrates
Choosing Factor Concentrates
Monitoring Response
Concerns With Prophylaxis
Is It Possible to Stop Prophylaxis?
Functional Assessment Tools
Objective Assessment: Imaging
Global Implications
Concluding Remarks
Abbreviations
Abbreviations (cont)