Predictors of Long-Term Clinical Outcome in Hurler Syndrome Patients after Successful Hematopoietic Cell Transplantation: An International Study  Mieke.

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Predictors of Long-Term Clinical Outcome in Hurler Syndrome Patients after Successful Hematopoietic Cell Transplantation: An International Study  Mieke Aldenhoven, MD, Paul Orchard, MD, Joanne Kurtzberg, MD, Robert Wynn, MD, Anne O'Meara, MD, Paul Veys, MD, Alain Fischer, MD, PhD, Vassili Valayannopoulos, MD, Benedicte Neven, MD, PhD, Attilio Rovelli, MD, Vinod K. Prasad, MD, Jakub Tolar, MD, PhD, Elsa Shapiro, PhD, Simon Jones, MD, Rossella Parini, MD, Marleen Renard, MD, Victoria Bordon, MD, Michele Poe, PhD, Tom de Koning, MD, PhD, Ed Wraith, MD, Maria Escolar, MD, Jaap-Jan Boelens, MD, PhD  Biology of Blood and Marrow Transplantation  Volume 20, Issue 2, Pages S78-S79 (February 2014) DOI: 10.1016/j.bbmt.2013.12.095 Copyright © 2014 Terms and Conditions

Figure 1 Cognitive development estimated by the cognitive status at HCT. Biology of Blood and Marrow Transplantation 2014 20, S78-S79DOI: (10.1016/j.bbmt.2013.12.095) Copyright © 2014 Terms and Conditions

Figure 2 Occurrence of surgical intervention for cord compression estimated by the obtained leukocyte IDUA enzyme level. Biology of Blood and Marrow Transplantation 2014 20, S78-S79DOI: (10.1016/j.bbmt.2013.12.095) Copyright © 2014 Terms and Conditions

Figure 3 Height estimated by the obtained leukocyte IDUA enzyme level. Biology of Blood and Marrow Transplantation 2014 20, S78-S79DOI: (10.1016/j.bbmt.2013.12.095) Copyright © 2014 Terms and Conditions