Successful in utero stem cell transplantation in X-linked severe combined immunodeficiency by Alessandra Magnani, Jean-Marie Jouannic, Jérémie Rosain,

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Presentation transcript:

Successful in utero stem cell transplantation in X-linked severe combined immunodeficiency by Alessandra Magnani, Jean-Marie Jouannic, Jérémie Rosain, Aurélie Gabrion, Fabien Touzot, Cécile Roudaut, Sven Kracker, Nizar Mahlaoui, Antoine Toubert, Emmanuel Clave, Elisabeth A. Macintyre, Isabelle Radford-Weiss, Marion Alcantara, Elisa Magrin, Brigitte Ternaux, Jennifer Nisoy, Laure Caccavelli, Anne-Marie Darras, Capucine Picard, Stéphane Blanche, and Marina Cavazzana BloodAdv Volume 3(3):237-241 February 12, 2019 © 2019 by The American Society of Hematology

Immune reconstitution after birth. Immune reconstitution after birth. (A) CD3+, CD4+, CD8+, CD31+CD45RA+CD4+, CD19+, and CD56+ cell counts. (B) Immunoglobulin A (IgA), IgM, and IgG reconstitution. (C) TRECs. Dots correspond to the values recorded. The lower and upper boundaries of the age-specific normal range are indicated by solid and dashed lines, respectively. Alessandra Magnani et al. Blood Adv 2019;3:237-241 © 2019 by The American Society of Hematology