1. Why Gene Therapy for Hemophilia?

2. This program will include a discussion of investigational agents not approved by the FDA for use in the United States

3. Introduction

4. Current Obstacles to Factor Replacement

5. What Gene Therapy May Look Like

6. Potential Benefits of Gene Therapy

7. Cautions Regarding Gene Therapy

8. Issues to Emphasize in Conversations With Patients

9. Unknowns of Gene Therapy

10. Safety

11. Treating Hemophilia in Countries With Limited Healthcare Resources

12. Assessing the Potential of Gene Therapy in Countries With Limited Resources

13. Concluding Remarks

14. Abbreviations