1. Volume 19, Issue 7, Pages 1193-1198 (July 2011)
Stem Cell Gene Therapy for Fanconi Anemia: Report from the 1st International Fanconi Anemia Gene Therapy Working Group Meeting 
Jakub Tolar, Jennifer E Adair, Michael Antoniou, Cynthia C Bartholomae, Pamela S Becker, Bruce R Blazar, Juan Bueren, Thomas Carroll, Marina Cavazzana-Calvo, D Wade Clapp, Robert Dalgleish, Anne Galy, H Bobby Gaspar, Helmut Hanenberg, Christof Von Kalle, Hans-Peter Kiem, Dirk Lindeman, Luigi Naldini, Susana Navarro, Raffaele Renella, Paula Rio, Julián Sevilla, Manfred Schmidt, Els Verhoeyen, John E Wagner, David A Williams, Adrian J Thrasher 
Molecular Therapy 
Volume 19, Issue 7, Pages (July 2011)
DOI: /mt
Copyright © 2011 The American Society of Gene & Cell Therapy Terms and Conditions

2. Figure 1
The lentiviral vector pC/RRL-PGK-FANCA-WPRE. CMV, cytomegalovirus; cPPT, central polypurine tract; FANCA, Fanconi anemia cDNA; PGK, phosphoglycerate kinase; RRE, rev responsive element; SA, splice acceptor; SD, splice donor; WPRE, safety-optimized version of the woodchuck hepatitis virus posttranscriptional regulatory element.
Molecular Therapy  , DOI: ( /mt )
Copyright © 2011 The American Society of Gene & Cell Therapy Terms and Conditions