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Genome-editing Technologies for Gene and Cell Therapy

Published byΠρίσκιλλα Φωτόπουλος Modified over 5 years ago

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Presentation on theme: "Genome-editing Technologies for Gene and Cell Therapy"— Presentation transcript:

1 Genome-editing Technologies for Gene and Cell Therapy
Morgan L Maeder, Charles A Gersbach  Molecular Therapy  Volume 24, Issue 3, Pages (March 2016) DOI: /mt Copyright © 2016 Official journal of the American Society of Gene & Cell Therapy Terms and Conditions

2 Figure 1 Mechanisms of double-strand break repair.
Molecular Therapy  , DOI: ( /mt ) Copyright © 2016 Official journal of the American Society of Gene & Cell Therapy Terms and Conditions

3 Figure 2 Common DNA targeting platforms for genome editing.
Molecular Therapy  , DOI: ( /mt ) Copyright © 2016 Official journal of the American Society of Gene & Cell Therapy Terms and Conditions

4 Figure 3 Ex vivo and in vivo strategies for therapeutic genome editing. Molecular Therapy  , DOI: ( /mt ) Copyright © 2016 Official journal of the American Society of Gene & Cell Therapy Terms and Conditions

5 Figure 4 Diversity of targets for therapeutic genome editing.
Molecular Therapy  , DOI: ( /mt ) Copyright © 2016 Official journal of the American Society of Gene & Cell Therapy Terms and Conditions

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