Presentation is loading. Please wait.

Presentation is loading. Please wait.

In utero stem cell transplantation and gene therapy: rationale, history, and recent advances toward clinical application  Graça Almeida-Porada, Anthony.

Published byRosalyn Robertson Modified over 5 years ago

Similar presentations

Presentation on theme: "In utero stem cell transplantation and gene therapy: rationale, history, and recent advances toward clinical application  Graça Almeida-Porada, Anthony."— Presentation transcript:

1 In utero stem cell transplantation and gene therapy: rationale, history, and recent advances toward clinical application  Graça Almeida-Porada, Anthony Atala, Christopher D Porada  Molecular Therapy - Methods & Clinical Development  Volume 3, (January 2016) DOI: /mtm Copyright © 2016 Official journal of the American Society of Gene & Cell Therapy Terms and Conditions

2 Figure 1 Overview of hematopoietic and immune events impacting IUTx and IUGT. Molecular Therapy - Methods & Clinical Development 2016 3, DOI: ( /mtm ) Copyright © 2016 Official journal of the American Society of Gene & Cell Therapy Terms and Conditions

Download ppt "In utero stem cell transplantation and gene therapy: rationale, history, and recent advances toward clinical application  Graça Almeida-Porada, Anthony."

Similar presentations

Gene Preference in Maple Syrup Urine Disease Mary M. Nellis, Dean J. Danner The American Journal of Human Genetics Volume 68, Issue 1, Pages 232-237 (January.

Gene Preference in Maple Syrup Urine Disease Mary M. Nellis, Dean J. Danner The American Journal of Human Genetics Volume 68, Issue 1, Pages (January.
Cell Traction Forces Direct Fibronectin Matrix Assembly Christopher A. Lemmon, Christopher S. Chen, Lewis H. Romer Biophysical Journal Volume 96, Issue.

Cell Traction Forces Direct Fibronectin Matrix Assembly Christopher A. Lemmon, Christopher S. Chen, Lewis H. Romer Biophysical Journal Volume 96, Issue.
A Simplified Procedure for Hematopoietic Stem Cell Amplification Using a Serum-Free, Feeder Cell-Free Culture System Ian M. Rogers, Nobuko Yamanaka, Robert.

A Simplified Procedure for Hematopoietic Stem Cell Amplification Using a Serum-Free, Feeder Cell-Free Culture System Ian M. Rogers, Nobuko Yamanaka, Robert.
Steven Joffe, Michelle M. Mello, E. Francis Cook, Stephanie J. Lee 

Steven Joffe, Michelle M. Mello, E. Francis Cook, Stephanie J. Lee 
Genetic Engineering and Manufacturing of Hematopoietic Stem Cells

Genetic Engineering and Manufacturing of Hematopoietic Stem Cells
Volume 20, Issue 2, (February 2012)

Volume 20, Issue 2, (February 2012)
Production and clinical development of nanoparticles for gene delivery

Production and clinical development of nanoparticles for gene delivery
414. A Novel Clinical Severity Scoring Measure in Canine X-Linked Myotubular Myopathy: Results Following Systemic AAV Gene Replacement    Molecular Therapy 

414. A Novel Clinical Severity Scoring Measure in Canine X-Linked Myotubular Myopathy: Results Following Systemic AAV Gene Replacement    Molecular Therapy 
209. Use of Helicobacter pyroli Neutrophil Activating Protein (NAP) as an Immune- Modulatory Agent To Enhance the Efficacy of Oncolytic Adenovirus Therapy.

209. Use of Helicobacter pyroli Neutrophil Activating Protein (NAP) as an Immune- Modulatory Agent To Enhance the Efficacy of Oncolytic Adenovirus Therapy.
Genome-editing Technologies for Gene and Cell Therapy

Genome-editing Technologies for Gene and Cell Therapy
How to Treat MDS without Stem Cell Transplantation

How to Treat MDS without Stem Cell Transplantation
Volume 20, Issue 3, Pages (March 2012)

Volume 20, Issue 3, Pages (March 2012)
627. Non-Invasive, Multimodal Imaging of Microvesicles with Metabolically Biotinylated, Membrane-Bound Gaussia Luciferase    Molecular Therapy  Volume.

627. Non-Invasive, Multimodal Imaging of Microvesicles with Metabolically Biotinylated, Membrane-Bound Gaussia Luciferase    Molecular Therapy  Volume.
Steven Joffe, Michelle M. Mello, E. Francis Cook, Stephanie J. Lee 

Steven Joffe, Michelle M. Mello, E. Francis Cook, Stephanie J. Lee 
162. Stability of Polymer/Plasmid DNA Complexes In Vitro and In Vivo

162. Stability of Polymer/Plasmid DNA Complexes In Vitro and In Vivo
281. Rapid Generation of Induced Pluripotent Stem Cells (iPSCs) from the Urine of a Patient with Duchenne Muscular Dystrophy    Molecular Therapy  Volume.

281. Rapid Generation of Induced Pluripotent Stem Cells (iPSCs) from the Urine of a Patient with Duchenne Muscular Dystrophy    Molecular Therapy  Volume.
Direct Conversion of Skin Cells into Blood: Alchemy or Science?

Direct Conversion of Skin Cells into Blood: Alchemy or Science?
Molecular Therapy  Volume 20, Pages S261-S262 (May 2012) DOI: /S (16)

Molecular Therapy  Volume 20, Pages S261-S262 (May 2012) DOI: /S (16)
Evolving Gene Therapy in Primary Immunodeficiency

Evolving Gene Therapy in Primary Immunodeficiency
Sam Afkhami, Yushi Yao, Zhou Xing 

Sam Afkhami, Yushi Yao, Zhou Xing 

Similar presentations

Ads by Google